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result sql = Anti-angiogenic strategies in medulloblastoma: reality or mystery?
Anti-angiogenic strategies in medulloblastoma: reality or mystery?
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result sql = Medulloblastoma is the most common malignant brain tumor of childhood. Surgery, radiation therapy and chemotherapy successfully cure many patients, but survivors can suffer long-term toxicities affecting their neurocognitive and growth potential; furthermore, there is no curative therapy in up to 30% of cases, mainly because of to our incomplete understanding of many of the underlying molecular and cellular processes. Angiogenesis is a hallmark of the progression of medulloblastoma and, over the last years, investigators have sought to develop effective and less toxic anti-angiogenic strategies, including the inhibition or destruction of abnormal blood vessels using either anti-angiogenic or vascular disrupting agents. However, the results are conflicting principally because of the complex biology of tumor vasculature and the irregular geometry of the vascular system in real space. In addition, current targets of anti-angiogenic therapy, such as vascular endothelial growth factor (VEGF), are thought to be critical for both physiological and pathological angiogenesis, and clinical side effects of anti-VEGF therapy are beginning to emerge. We here review the state-of-the-art concerning anti-angiogenic targets for medulloblastoma treatment, and discuss the complexity of the vascular system that intrinsically limits the efficacy of current strategies.

Publication: Pediatr. Res. 2008 Jan 24 ;:.
Publication Date: 2008 Jan 24
Study Author(s): Grizzi, Fabio;Weber, Christina;Di Ieva, Antonio;
Institution: Laboratories of Quantitative Medicine [F.G.], Department of Neurosurgery [A.I.], Istituto Clinico Humanitas IRCCS, 20089 Rozzano, Milan, Italy; Regional Hospital [C.W.], A-6800 Feldkirch, Austria.
Shortcut link to this study:
Medulloblastoma is the most common malignant brain tumor of childhood. Surgery, radiation therapy and chemotherapy successfully cure many patients, but survivors can suffer long-term toxicities affecting their neurocognitive and growth potential; furthermore, there is no curative therapy in up to 30% of cases, mainly because of to our incomplete understanding of many of the underlying molecular and cellular processes. Angiogenesis is a hallmark of the progression of medulloblastoma and, over the last years, investigators have sought to develop effective and less toxic anti-angiogenic strategies, including the inhibition or destruction of abnormal blood vessels using either anti-angiogenic or vascular disrupting agents. However, the results are conflicting principally because of the complex biology of tumor vasculature and the irregular geometry of the vascular system in real space. In addition, current targets of anti-angiogenic therapy, such as vascular endothelial growth factor (VEGF), are thought to be critical for both physiological and pathological angiogenesis, and clinical side effects of anti-VEGF therapy are beginning to emerge. We here review the state-of-the-art concerning anti-angiogenic targets for medulloblastoma treatment, and discuss the complexity of the vascular system that intrinsically limits the efficacy of current strategies.
PMID: 18319648

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